Cas13-Mediated RNA Base Editing for the Treatment of Hereditary Hypertrophic Cardiomyopathy

Qun Hu

Jiajia Lin

Haodong Cui

Xin Zhao

Meixian Wu

HuidaGene Therapeutics Inc, Shanghai, China (M.W., H.Y., G.L.).

Shuping Wei

Zhongshan Institute for Drug Discovery, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, China (Q.H., H.C., X.Z., S.W., M.D., B.W., T.L., X.G., Q.H., Y.L., S.L., H.Y., H.-B.-L., G.L.).

Min Deng

Bingyan Wang

Tan Liu

Xiaori Gao

Zhongshan Institute for Drug Discovery, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, China (Q.H., H.C., X.Z., S.W., M.D., B.W., T.L., X.G., Q.H., Y.L., S.L., H.Y., H.-B.-L., G.L.).

Qiuying Huang

College of Materials Science and Engineering

Yutao Liang

Zhongshan Institute for Drug Discovery, Shanghai Institute of Materia Medica, Chinese Academy of Sciences

Simiao Liu

Hui Yang

Han-Bin Lin

Zhongshan Institute for Drug Discovery, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, China (Q.H., H.C., X.Z., S.W., M.D., B.W., T.L., X.G., Q.H., Y.L., S.L., H.Y., H.-B.-L., G.L.).

Guoling Li