Cardiotoxic Effects and Microdystrophin Expression after Gene Therapy for DMD
Article Details
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
Authors (28)
Benjamin J. Samelson-Jones
Children’s Hospital of Philadelphia, Philadelphia
Cristina Martos-Rus
Children’s Hospital of Philadelphia, Philadelphia
Carolyn M. Yrigollen
Children’s Hospital of Philadelphia, Philadelphia
Luis Tecedor
Children’s Hospital of Philadelphia, Philadelphia
Juliana C. Small
Children’s Hospital of Philadelphia, Philadelphia
Susan E. Matesanz
Children’s Hospital of Philadelphia, Philadelphia
Connor T. Watson
Children’s Hospital of Philadelphia, Philadelphia
Andrew R. Vanden Heuvel
Children’s Hospital of Philadelphia, Philadelphia
Sean Carrig
Children’s Hospital of Philadelphia, Philadelphia
Sabrina W. Yum
Children’s Hospital of Philadelphia, Philadelphia
John F. Brandsema
Children’s Hospital of Philadelphia, Philadelphia
Kimberly Lin
Children’s Hospital of Philadelphia, Philadelphia
Carol Wittlieb-Weber
Children’s Hospital of Philadelphia, Philadelphia
Angela N. Viaene
Pierre P. Russo
Children’s Hospital of Philadelphia, Philadelphia
Sara Partington
University of Pennsylvania, Philadelphia
Katie Huynh
Children’s Hospital of Philadelphia, Philadelphia
Tiffany Seneviratne
Children’s Hospital of Philadelphia, Philadelphia
Silvia Juarez Rojas
Emory University School of Medicine, Atlanta
Bhavya S. Doshi
Emory University School of Medicine, Atlanta
Perry Shieh
Kevin M. Flanigan
Nationwide Children’s Hospital, Columbus, OH
Emma Frair
Nationwide Children’s Hospital, Columbus, OH
Stefan Nicolau
Nationwide Children’s Hospital, Columbus, OH
Michael W. Lawlor
Diverge Translational Science Laboratory, Milwaukee
Julie M. Crudele
University of Washington School of Medicine, Seattle
Beverly L. Davidson
Raymond G. Perelman Center for Cellular and Molecular Therapeutics, The Children’s Hospital of Philadelphia, University of Pennsylvania
Lindsey A. George
Children’s Hospital of Philadelphia, Philadelphia