Cardiotoxic Effects and Microdystrophin Expression after Gene Therapy for DMD

B Benjamin J. Samelson-Jones (Children’s Hospital of Philadelphia, Philadelphia) C Cristina Martos-Rus (Children’s Hospital of Philadelphia, Philadelphia) C Carolyn M. Yrigollen (Children’s Hospital of Philadelphia, Philadelphia) L Luis Tecedor (Children’s Hospital of Philadelphia, Philadelphia) J Juliana C. Small (Children’s Hospital of Philadelphia, Philadelphia) S Susan E. Matesanz (Children’s Hospital of Philadelphia, Philadelphia) C Connor T. Watson (Children’s Hospital of Philadelphia, Philadelphia) A Andrew R. Vanden Heuvel (Children’s Hospital of Philadelphia, Philadelphia) S Sean Carrig (Children’s Hospital of Philadelphia, Philadelphia) S Sabrina W. Yum (Children’s Hospital of Philadelphia, Philadelphia) J John F. Brandsema (Children’s Hospital of Philadelphia, Philadelphia) K Kimberly Lin (Children’s Hospital of Philadelphia, Philadelphia) C Carol Wittlieb-Weber (Children’s Hospital of Philadelphia, Philadelphia) A Angela N. Viaene P Pierre P. Russo (Children’s Hospital of Philadelphia, Philadelphia) S Sara Partington (University of Pennsylvania, Philadelphia) K Katie Huynh (Children’s Hospital of Philadelphia, Philadelphia) T Tiffany Seneviratne (Children’s Hospital of Philadelphia, Philadelphia) S Silvia Juarez Rojas (Emory University School of Medicine, Atlanta) B Bhavya S. Doshi (Emory University School of Medicine, Atlanta) P Perry Shieh K Kevin M. Flanigan (Nationwide Children’s Hospital, Columbus, OH) E Emma Frair (Nationwide Children’s Hospital, Columbus, OH) S Stefan Nicolau (Nationwide Children’s Hospital, Columbus, OH) M Michael W. Lawlor (Diverge Translational Science Laboratory, Milwaukee) J Julie M. Crudele (University of Washington School of Medicine, Seattle) B Beverly L. Davidson (Raymond G. Perelman Center for Cellular and Molecular Therapeutics, The Children’s Hospital of Philadelphia, University of Pennsylvania) L Lindsey A. George (Children’s Hospital of Philadelphia, Philadelphia)

Article Details

Volume / Issue Vol. 1, Issue 1
Published July 22, 2026
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (28)

B

Benjamin J. Samelson-Jones

Children’s Hospital of Philadelphia, Philadelphia

C

Cristina Martos-Rus

Children’s Hospital of Philadelphia, Philadelphia

C

Carolyn M. Yrigollen

Children’s Hospital of Philadelphia, Philadelphia

L

Luis Tecedor

Children’s Hospital of Philadelphia, Philadelphia

J

Juliana C. Small

Children’s Hospital of Philadelphia, Philadelphia

S

Susan E. Matesanz

Children’s Hospital of Philadelphia, Philadelphia

C

Connor T. Watson

Children’s Hospital of Philadelphia, Philadelphia

A

Andrew R. Vanden Heuvel

Children’s Hospital of Philadelphia, Philadelphia

S

Sean Carrig

Children’s Hospital of Philadelphia, Philadelphia

S

Sabrina W. Yum

Children’s Hospital of Philadelphia, Philadelphia

J

John F. Brandsema

Children’s Hospital of Philadelphia, Philadelphia

K

Kimberly Lin

Children’s Hospital of Philadelphia, Philadelphia

C

Carol Wittlieb-Weber

Children’s Hospital of Philadelphia, Philadelphia

A

Angela N. Viaene

P

Pierre P. Russo

Children’s Hospital of Philadelphia, Philadelphia

S

Sara Partington

University of Pennsylvania, Philadelphia

K

Katie Huynh

Children’s Hospital of Philadelphia, Philadelphia

T

Tiffany Seneviratne

Children’s Hospital of Philadelphia, Philadelphia

S

Silvia Juarez Rojas

Emory University School of Medicine, Atlanta

B

Bhavya S. Doshi

Emory University School of Medicine, Atlanta

P

Perry Shieh

K

Kevin M. Flanigan

Nationwide Children’s Hospital, Columbus, OH

E

Emma Frair

Nationwide Children’s Hospital, Columbus, OH

S

Stefan Nicolau

Nationwide Children’s Hospital, Columbus, OH

M

Michael W. Lawlor

Diverge Translational Science Laboratory, Milwaukee

J

Julie M. Crudele

University of Washington School of Medicine, Seattle

B

Beverly L. Davidson

Raymond G. Perelman Center for Cellular and Molecular Therapeutics, The Children’s Hospital of Philadelphia, University of Pennsylvania

L

Lindsey A. George

Children’s Hospital of Philadelphia, Philadelphia