Branched endosomal disruptor (BEND) lipids mediate delivery of mRNA and CRISPR-Cas9 ribonucleoprotein complex for hepatic gene editing and T cell engineering

M Marshall S. Padilla (Department of Bioengineering) K Kaitlin Mrksich Y Yiming Wang R Rebecca M. Haley J Jacqueline J. Li (Department of Bioengineering) E Emily L. Han R Rakan El-Mayta E Emily H. Kim (Department of Biology, University of Florida) S Sofia Dias N Ningqiang Gong (Department of Bioengineering, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States) S Sridatta V. Teerdhala X Xuexiang Han V Vivek Chowdhary (Gene Therapy Program, Perelman School of Medicine, University of Pennsylvania) L Lulu Xue (Department of Bioengineering, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States) Z Zain Siddiqui H Hannah M. Yamagata (Department of Bioengineering) D Dongyoon Kim (Department of Bioengineering) I Il-Chul Yoon (Department of Bioengineering, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States) J James M. Wilson (Gene Therapy Program, Perelman School of Medicine, University of Pennsylvania) R Ravi Radhakrishnan M Michael J. Mitchell

Article Details

Volume / Issue Vol. 16, Issue 1
Published January 24, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (21)

M

Marshall S. Padilla

Department of Bioengineering

K

Kaitlin Mrksich

Y

Yiming Wang

R

Rebecca M. Haley

J

Jacqueline J. Li

Department of Bioengineering

E

Emily L. Han

R

Rakan El-Mayta

E

Emily H. Kim

Department of Biology, University of Florida

S

Sofia Dias

N

Ningqiang Gong

Department of Bioengineering, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States

S

Sridatta V. Teerdhala

X

Xuexiang Han

V

Vivek Chowdhary

Gene Therapy Program, Perelman School of Medicine, University of Pennsylvania

L

Lulu Xue

Department of Bioengineering, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States

Z

Zain Siddiqui

H

Hannah M. Yamagata

Department of Bioengineering

D

Dongyoon Kim

Department of Bioengineering

I

Il-Chul Yoon

Department of Bioengineering, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States

J

James M. Wilson

Gene Therapy Program, Perelman School of Medicine, University of Pennsylvania

R

Ravi Radhakrishnan

M

Michael J. Mitchell