BET inhibition blunts antibody production and macrophage-mediated fibrosis to restore lung function in murine cGVHD

R Rathan Kumar (The Ohio State University, Columbus, Ohio, United States) L Lotus Neidemire-Colley (The Ohio State University, Columbus, Ohio, United States) E Elizabeth A. R. Garfinkle (3Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, OH) C Camryn Steere (The Ohio State University, COLUMBUS, Ohio, United States) S Simran Surana (1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH) A Annie Murray G Giorgia Giordano (The Ohio State University, United States) O Olivia Martin (1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH) E Emerson D. Woodbury (4Division of Cardiac Surgery, Department of Surgery, The Ohio State University, Columbus, OH) A Adithe Rivaldi (Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States) S Satishkumar Singh (1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH) K Kara Corps K Katlyn Lederer (6Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA) M Malith Karunasiri (The Ohio State University, Columbus, Ohio, United States) M Matthew W. Gorr L Loren E. Wold L Lalit Sehgal K Kenneth J. Oestreich N Nicole R. Grieselhuber (1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH) M Marcos J. de Lima (1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH) B Bruce R. Blazar (Department of Pediatrics, Division of Blood & Marrow Transplant & Cellular Therapy, University of Minnesota) I Ivan Maillard K Katherine E. Miller H Hannah K. Choe (1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH) P Parvathi Ranganathan (Ohio State University, Columbus, Ohio, United States)

Abstract

Abstract Chronic graft-versus-host disease (cGVHD) significantly contributes to late mortality after allogeneic stem cell transplantation, with bronchiolitis obliterans syndrome (BOS) being a particularly lethal and treatment-resistant complication despite available therapies. Bromodomain and extraterminal (BET) proteins are epigenetic readers driving inflammatory transcriptional programs across multiple cell types. We hypothesized that BET inhibition would suppress inflammatory T and B cells and decrease macrophage polarization to a profibrotic phenotype, alleviating disease. In an established BOS cGVHD model, BET inhibition reduced germinal center (GC) formation and responses through a reduction of the CXCL13:CXCR5 axis and inflammatory T follicular helper/GC B cells in the spleen, along with a reduction in plasma cell infiltration within the lung. Mice with cGVHD had elevated pathogenic immunoglobulin G1 (IgG1) and IgM levels, both in circulation and deposited on lung tissue, which were attenuated under BET inhibition. Single-cell RNA-sequencing analysis revealed distinct cell states in the BOS lung vs control. In cGVHD mice, gene set enrichment analysis revealed the upregulation of profibrotic Arginase1 and Tgfb1 expression in alveolar macrophages (AM) and interstitial macrophages (IM), which was significantly reduced with BET inhibition. Furthermore, BET inhibition targeted lung-infiltrating M2 macrophages through the selective depletion of CD206+FcγR+ IM and AM, ultimately resulting in reduced collagen deposition and improved lung function. Our findings reveal a previously unrecognized mechanistic axis of BET regulation during cGVHD fibrosis and highlight BET inhibition as a promising therapeutic strategy.

Article Details

Journal Blood
Volume / Issue Vol. 147, Issue 23
Published June 04, 2026
Pages 2828-2844
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (25)

R

Rathan Kumar

The Ohio State University, Columbus, Ohio, United States

L

Lotus Neidemire-Colley

The Ohio State University, Columbus, Ohio, United States

E

Elizabeth A. R. Garfinkle

3Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, OH

C

Camryn Steere

The Ohio State University, COLUMBUS, Ohio, United States

S

Simran Surana

1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH

A

Annie Murray

G

Giorgia Giordano

The Ohio State University, United States

O

Olivia Martin

1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH

E

Emerson D. Woodbury

4Division of Cardiac Surgery, Department of Surgery, The Ohio State University, Columbus, OH

A

Adithe Rivaldi

Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States

S

Satishkumar Singh

1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH

K

Kara Corps

K

Katlyn Lederer

6Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA

M

Malith Karunasiri

The Ohio State University, Columbus, Ohio, United States

M

Matthew W. Gorr

L

Loren E. Wold

L

Lalit Sehgal

K

Kenneth J. Oestreich

N

Nicole R. Grieselhuber

1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH

M

Marcos J. de Lima

1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH

B

Bruce R. Blazar

Department of Pediatrics, Division of Blood & Marrow Transplant & Cellular Therapy, University of Minnesota

I

Ivan Maillard

K

Katherine E. Miller

H

Hannah K. Choe

1Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH

P

Parvathi Ranganathan

Ohio State University, Columbus, Ohio, United States