BCMA-directed CAR-T cell therapy induces durable drug-free remission in refractory primary immune thrombocytopenia

J Jinhui Shu (Institute of Hematology, Union Hospital, Tongji Medical College, Huazhong University of Science and Technology, Wuhan, China) M Min Xu P Peiru Li (Institute of Hematology, Union Hospital, Tongji Medical College, Huazhong University of Science and Technology, Wuhan, China) W Wei Xie L Lin Liu H Hongjian Li J James B. Bussel (Department of Pediatrics, Division of Hematology/Oncology, Weill Cornell Medicine, New York, New York, United States) Y Yu Hu H Heng Mei (Institute of Hematology, Union Hospital, Tongji Medical College, Huazhong University of Science and Technology; Hubei Provincial Clinical Medical Center of Cell Therapy for Neoplastic Disease, Wuhan, China)

Abstract

This first clinical evaluation of BCMA CAR-T cell therapy in four patients with refractory primary ITP demonstrated manageable safety, rapid and sustained platelet recovery, and durable drug-free complete remission lasting up to 15 months, supporting further evaluation in larger studies.

Article Details

Journal Blood
Volume / Issue Vol. 1, Issue 1
Published July 24, 2026
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (9)

J

Jinhui Shu

Institute of Hematology, Union Hospital, Tongji Medical College, Huazhong University of Science and Technology, Wuhan, China

M

Min Xu

P

Peiru Li

Institute of Hematology, Union Hospital, Tongji Medical College, Huazhong University of Science and Technology, Wuhan, China

W

Wei Xie

L

Lin Liu

H

Hongjian Li

J

James B. Bussel

Department of Pediatrics, Division of Hematology/Oncology, Weill Cornell Medicine, New York, New York, United States

Y

Yu Hu

H

Heng Mei

Institute of Hematology, Union Hospital, Tongji Medical College, Huazhong University of Science and Technology; Hubei Provincial Clinical Medical Center of Cell Therapy for Neoplastic Disease, Wuhan, China