Base Editing of <i>HBG1</i> and <i>HBG2</i> Promoters for Sickle Cell Disease

A Ashish O. Gupta (University of Minnesota, Minneapolis) A Akshay Sharma H Haydar Frangoul (Sarah Cannon Research Institute at the Children’s Hospital at TriStar Centennial, Nashville) J Julie Kanter M Markus Y. Mapara (Columbia University Medical Center, New York) J Jignesh Dalal (Rainbow Babies and Children’s Hospital, Cleveland) A Asif Alavi (Henry Ford Health System, Detroit) J Jennifer J. Jaroscak (Medical University of South Carolina, Charleston) E Ernesto Ayala (Mayo Clinic, Jacksonville, FL) J John F. DiPersio (Department of Medicine, Washington University School of Medicine, St. Louis) E Edward D. Ziga (University of Miami, Miami) M Mary Eapen (Medical College of Wisconsin, Milwaukee) S Stacey Rifkin-Zenenberg (Hackensack University Medical Center, Hackensack, NJ) A Alex C. Minella (Beam Therapeutics, Cambridge, MA) Y Yinzhong Chen (Beam Therapeutics, Cambridge, MA) S Sarah Chesler (Beam Therapeutics, Cambridge, MA) S Srikanth Ambati (Beam Therapeutics, Cambridge, MA) T Thomas S. Bowman (Beam Therapeutics, Cambridge, MA) B Bahru Habtemariam (Beam Therapeutics, Cambridge, MA) M Marcelyne Joseney-Antoine (Beam Therapeutics, Cambridge, MA) P Priya S. Chockalingam (Beam Therapeutics, Cambridge, MA) L Ling Lin (Department of Psychiatry and Behavioral Sciences, Center for Sleep Sciences and Medicine, Stanford University) S Sunita Goyal (Beam Therapeutics, Cambridge, MA) A Amy Simon (Beam Therapeutics, Cambridge, MA) A Alexis A. Thompson (Children’s Hospital of Philadelphia, Philadelphia) M Matthew M. Heeney (Dana–Farber/Boston Children’s Cancer and Blood Disorders Center, Boston)

Article Details

Volume / Issue Vol. 394, Issue 18
Published May 07, 2026
Pages 1824-1835
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (26)

A

Ashish O. Gupta

University of Minnesota, Minneapolis

A

Akshay Sharma

H

Haydar Frangoul

Sarah Cannon Research Institute at the Children’s Hospital at TriStar Centennial, Nashville

J

Julie Kanter

M

Markus Y. Mapara

Columbia University Medical Center, New York

J

Jignesh Dalal

Rainbow Babies and Children’s Hospital, Cleveland

A

Asif Alavi

Henry Ford Health System, Detroit

J

Jennifer J. Jaroscak

Medical University of South Carolina, Charleston

E

Ernesto Ayala

Mayo Clinic, Jacksonville, FL

J

John F. DiPersio

Department of Medicine, Washington University School of Medicine, St. Louis

E

Edward D. Ziga

University of Miami, Miami

M

Mary Eapen

Medical College of Wisconsin, Milwaukee

S

Stacey Rifkin-Zenenberg

Hackensack University Medical Center, Hackensack, NJ

A

Alex C. Minella

Beam Therapeutics, Cambridge, MA

Y

Yinzhong Chen

Beam Therapeutics, Cambridge, MA

S

Sarah Chesler

Beam Therapeutics, Cambridge, MA

S

Srikanth Ambati

Beam Therapeutics, Cambridge, MA

T

Thomas S. Bowman

Beam Therapeutics, Cambridge, MA

B

Bahru Habtemariam

Beam Therapeutics, Cambridge, MA

M

Marcelyne Joseney-Antoine

Beam Therapeutics, Cambridge, MA

P

Priya S. Chockalingam

Beam Therapeutics, Cambridge, MA

L

Ling Lin

Department of Psychiatry and Behavioral Sciences, Center for Sleep Sciences and Medicine, Stanford University

S

Sunita Goyal

Beam Therapeutics, Cambridge, MA

A

Amy Simon

Beam Therapeutics, Cambridge, MA

A

Alexis A. Thompson

Children’s Hospital of Philadelphia, Philadelphia

M

Matthew M. Heeney

Dana–Farber/Boston Children’s Cancer and Blood Disorders Center, Boston