Anti-CD19 chimeric antigen receptor T-cells therapy (CAR-T) is effective in secondary cns lymphoma (SCNSL) refractory to high-dose methotrexate (HDMTX)-based chemotherapy

P Piera Angelillo (10IRCCS San Raffaele Scientific Institute, Milan, Italy) E Edoardo Campodonico (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) T Teresa Calimeri (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) A Alice Di Rocco (6Division of Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy) A Alessia Castellino (20Division of Hematology - AO S. Croce e Carle, Cuneo and Laboratory of Blood Tumor Immunology, Molecular Biotechnology Center “Guido Tarone”, University of Torino, Cuneo, Italy) A Andrea Ferrario (4ASST Sette Laghi Ospedale di Circolo, UOC Ematologia, Varese, Italy) M Melania Celli (5Ospedale Infermi, UO Ematologia, Rimini, Italy) A Andrea Assanelli (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) L Lorenzo Lazzari (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) M Maria Teresa Lupo Stanghellini (IRCCS San Raffaele Scientific Institute, Italy) J Jacopo Peccatori (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) L Livia Donzelli (2Università Sapienza Roma, Hematology, Department of Translational and Precision Medicine, Rome, Italy) C Claudia Castellino (3Division of Hematology, Azienda Ospedaliera S. Croce e Carle, Cuneo, Italy) A Angela Genchi (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) N Nicoletta Anzalone (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) P Paolo Vezzulli (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) F Federico Fallanca (4IRCCS San Raffaele Scientific Institute, Milan, Italy) F Francesco Ancona (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) A Alessandro Bruno (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) G Giulio Cassanello (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) M Milena Coppola (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) F Federico Erbella (1IRCCS San Raffaele Scientific Institute, Strategic Program on Lymphomas, Milano, Italy) P Paolo Fiore (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) E Elena Flospergher (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) C Camilla Gariazzo (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) F Filippo Magri (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) F Fabrizio Marino (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) S Sarah Marktel S Sara Mastaglio (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) G Giovanni Matassa (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) R Raffaella Milani (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) R Rosamaria Nitti (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) M Madddalena Noviello (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) A Alessia Orsini (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) F Fanny Palumbo (1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy) A Annalisa Ruggeri (8San Raffaele Scientific Institute, Milan, Italy) F Fabio Ciceri (Vita-Salute San Raffaele University, Milan) A Andrés José María Ferreri (19IUniversity Vita-Salute San Raffaele, Milano, Italy Strategic Program on Lymphomas, IRCCS San Raffaele Scientific Institute, Milano, Italy, Milan, Italy)

Abstract

Abstract Introduction: Secondary involvement of the CNS is a direful complication of large B cell lymphomas (LBCL), which can occur at diagnosis or relapse. Treatment of SCNSL differs from systemic lymphomas and is based on high dose chemotherapy (CHT) with drugs that penetrate the blood-brain barrier, HDMTX in particular, followed by autologous stem cell transplantation (ASCT). However, 60% of pts is refractory to or relapses after this treatment, 2/3 of relapsed pts do not receive further salvage therapy, and responses are anecdotal. CAR-T is an effective salvage treatment for LBCL whereas experience in SCNSL is limited to a few registry studies, where response to prior lines and the number of SCNSL pts who result unsuitable candidates for CAR-T is roughly reported. Herein we report selection and management of consecutive pts with SCNSL referred to 3 Italian CAR-T-cell centres, providing more detailed information for pts who actually received CAR-T. Methods: SCNSL pts were evaluated for CAR-T eligibility between 07/22 and 03/25. Selected pts were offered a holding therapy according to extension of disease and prior treatments. Pts in CNS remission after holding were evaluated for CAR-T eligibility by a multidisciplinary team of experts. Eligible candidates underwent lymphocytoapheresis (Flu-Cy) and bridging therapy until commercial CAR-T infusion. Results: 23 pts were referred to holding: 6 partial-brain irradiation, 4 intrathecal CHT, 2 polatuzumab vedotin, 5 ibrutinib, 1 HD-ifosfamide-based CHT, 2 MATRix regimen, 1 thiotepa-based ASCT, combinations of these strategies in 2. 7 pts experienced progressive disease after holding, were deemed not eligible for CAR-T and died within one month. The other 16 achieved a remission of CNS disease and were eligible for CAR-T. All pts had ECOG 0-1, and all but one were refractory to prior HDMTX. Only one pt experienced G3-4 CRS, all CRS cases were successfully treated with tocilizumab and steroids, anakinra was used in 2 cases. ICANS were treated with steroids, plus anakinra in 2 cases. G≥3 ICANS occurs in two pts: one required pre-emptive ICU admission but resolved after 3 days, while the second pt had G1 CRS, developed refractory epilepticus status, and died 18 days after CAR-T infusion. Although recommended washout period was respected, the latter event could be explained by multiple intrathecal CHT instillations performed before CAR-T. Four pts had ≥1 cytopenia at 3 months. At a median follow up of 8 months (IQR: 3-12), 12/16 infused pts remain relapse-free; 3 had a systemic relapse, while none experienced CNS recurrence. Conclusion: Varied presentation and high aggressivity of SCNSL impede the use of a uniform treatment for these pts. SCNSL refractory to HDMTX-based polyCHT can benefit significantly from a tailored multimodal holding based on the pt's history and extension of disease. Only pts with good PS and responsive to holding therapy should be offered CAR-T to avoid superfluous toxicity.

Article Details

Journal Blood
Volume / Issue Vol. 146, Issue Supplement 1
Published November 03, 2025
Pages 7241-7241
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (38)

P

Piera Angelillo

10IRCCS San Raffaele Scientific Institute, Milan, Italy

E

Edoardo Campodonico

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

T

Teresa Calimeri

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

A

Alice Di Rocco

6Division of Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy

A

Alessia Castellino

20Division of Hematology - AO S. Croce e Carle, Cuneo and Laboratory of Blood Tumor Immunology, Molecular Biotechnology Center “Guido Tarone”, University of Torino, Cuneo, Italy

A

Andrea Ferrario

4ASST Sette Laghi Ospedale di Circolo, UOC Ematologia, Varese, Italy

M

Melania Celli

5Ospedale Infermi, UO Ematologia, Rimini, Italy

A

Andrea Assanelli

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

L

Lorenzo Lazzari

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

M

Maria Teresa Lupo Stanghellini

IRCCS San Raffaele Scientific Institute, Italy

J

Jacopo Peccatori

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

L

Livia Donzelli

2Università Sapienza Roma, Hematology, Department of Translational and Precision Medicine, Rome, Italy

C

Claudia Castellino

3Division of Hematology, Azienda Ospedaliera S. Croce e Carle, Cuneo, Italy

A

Angela Genchi

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

N

Nicoletta Anzalone

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

P

Paolo Vezzulli

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

F

Federico Fallanca

4IRCCS San Raffaele Scientific Institute, Milan, Italy

F

Francesco Ancona

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

A

Alessandro Bruno

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

G

Giulio Cassanello

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

M

Milena Coppola

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

F

Federico Erbella

1IRCCS San Raffaele Scientific Institute, Strategic Program on Lymphomas, Milano, Italy

P

Paolo Fiore

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

E

Elena Flospergher

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

C

Camilla Gariazzo

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

F

Filippo Magri

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

F

Fabrizio Marino

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

S

Sarah Marktel

S

Sara Mastaglio

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

G

Giovanni Matassa

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

R

Raffaella Milani

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

R

Rosamaria Nitti

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

M

Madddalena Noviello

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

A

Alessia Orsini

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

F

Fanny Palumbo

1San Raffaele Scientific Institute, Lymphoma Unit, Milan, Italy

A

Annalisa Ruggeri

8San Raffaele Scientific Institute, Milan, Italy

F

Fabio Ciceri

Vita-Salute San Raffaele University, Milan

A

Andrés José María Ferreri

19IUniversity Vita-Salute San Raffaele, Milano, Italy Strategic Program on Lymphomas, IRCCS San Raffaele Scientific Institute, Milano, Italy, Milan, Italy