AAV9-Mediated TNPO3 Overexpression in the Heart Rescues RBM20 Cardiomyopathy in Mice

J Julia Kornienko (Genome Biology Unit, European Molecular Biology Laboratory (EMBL), Heidelberg, Germany (J.K., L.S., K.F., L.M.S.).) L Laura Schraft (Genome Biology Unit, European Molecular Biology Laboratory (EMBL), Heidelberg, Germany (J.K., L.S., K.F., L.M.S.).) K Kai Fenzl M Maarten M.G. van den Hoogenhof (DZHK (German Centre for Cardiovascular Research), partner site Heidelberg/Mannheim, Heidelberg, Germany (J.K., K.F., M.M.G.v.d.H., L.M.S.).) L Lars M. Steinmetz

Article Details

Journal Circulation
Volume / Issue Vol. 152, Issue 10
Published September 09, 2025
Pages 739-742
ISSN 0009-7322
Publisher Lippincott Williams & Wilkins

Journal Info

Circulation

Lippincott Williams & Wilkins

ISSN: 0009-7322 Health Sciences

Authors (5)

J

Julia Kornienko

Genome Biology Unit, European Molecular Biology Laboratory (EMBL), Heidelberg, Germany (J.K., L.S., K.F., L.M.S.).

L

Laura Schraft

Genome Biology Unit, European Molecular Biology Laboratory (EMBL), Heidelberg, Germany (J.K., L.S., K.F., L.M.S.).

K

Kai Fenzl

M

Maarten M.G. van den Hoogenhof

DZHK (German Centre for Cardiovascular Research), partner site Heidelberg/Mannheim, Heidelberg, Germany (J.K., K.F., M.M.G.v.d.H., L.M.S.).

L

Lars M. Steinmetz