AAV9-mediated MYBPC3 gene therapy with optimized expression cassette enhances cardiac function and survival in MYBPC3 cardiomyopathy models

A Amara Greer-Short A Anna Greenwood E Elena C. Leon T Tawny Neal Qureshi K Konor von Kraut J Justin Wong J Jonathan H. Tsui C Christopher A. Reid Z Ze Cheng E Emilee Easter J Jin Yang J Jaclyn Ho S Stephanie Steltzer A Ana Budan M Marie Cho R Rishikesan Chandrakumar O Olga Cisne-Thompson C Charles Feathers T Tae Won Chung N Neshel Rodriguez S Samantha Jones C Chris Alleyne-Levy J Jun Liu F Frank Jing W William S. Prince J JianMin Lin K Kathryn N. Ivey W Whittemore G. Tingley T Timothy Hoey L Laura M. Lombardi

Article Details

Volume / Issue Vol. 16, Issue 1
Published March 04, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (30)

A

Amara Greer-Short

A

Anna Greenwood

E

Elena C. Leon

T

Tawny Neal Qureshi

K

Konor von Kraut

J

Justin Wong

J

Jonathan H. Tsui

C

Christopher A. Reid

Z

Ze Cheng

E

Emilee Easter

J

Jin Yang

J

Jaclyn Ho

S

Stephanie Steltzer

A

Ana Budan

M

Marie Cho

R

Rishikesan Chandrakumar

O

Olga Cisne-Thompson

C

Charles Feathers

T

Tae Won Chung

N

Neshel Rodriguez

S

Samantha Jones

C

Chris Alleyne-Levy

J

Jun Liu

F

Frank Jing

W

William S. Prince

J

JianMin Lin

K

Kathryn N. Ivey

W

Whittemore G. Tingley

T

Timothy Hoey

L

Laura M. Lombardi