Duan, C., Rong, S., Buerer, L., Neil, C. R., Zhong, Y., Lyu, Z., Savatt, J. M., Strande, N. T., Fairbrother, W. G. (2025). Single antisense oligonucleotides correct diverse splicing mutations in hotspot exons. Proceedings of the National Academy of Sciences. https://doi.org/10.1073/pnas.2425659122