Masanori Yoshida, Senthil Bhoopalan, Tsutomu Toki, Rika Kanezaki, Lili Kotmayer, Michelle Boals, Damian Krzyzanowski, Nishi Harwani, Paola Quarello, Ugo Ramenghi, Saskia Langemeijer, Ilja Diets, Kiminori Terui, Jason Farrar, Nathan Gray, Etsuro Ito, Marcin Wlodarski. "Polyclonal somatic gene rescue via uniparental disomy confers multilineage hematopoietic potential in treatment-independent patients with DBA syndrome." Blood, 2025. doi:10.1182/blood-2025-746