Phase 1 Study of AAV9.LAMP2B Gene Therapy in Danon Disease - Barry Greenberg; Matthew Taylor; Eric Adler; Steven Colan; David Ricks; Paul Yarabe; Pavan Battiprolu; Gaurav Shah; Kinnari Patel; Matthew Coggins; Susanna Carou-Keenan; Jonathan D. Schwartz; et al. (New England Journal of Medicine, 2025)