Xiupeng Chen, Qing Xie, Sarah J. Nath, Mojiao Tang, Hong Ma, Yasemin Özgür Günes, Tapan Sharma, Hao Liu, MengTian Cui, Ailing Du, Mengjia Lu, Sophia Y. Liu, Boonying Wassamon, Mengyao Xu, Joseph Yunxi Wu, Qin Su, Timothy P. Fitzgibbons, Jinghua Liu, Fang Wan, Veena Kumanan, Ran He, Yijie Ma, Jun Yang, Heather L. Gray-Edwards, Thomas L. Gallagher, Phillip W. L. Tai, Guangping Gao, Jun Xie. "Long-term comparative analysis of AAV9-mediated gene replacement therapies for spinal muscular atrophy in mice." Nature Communications, 2026. doi:10.1038/s41467-026-73545-8