Rasko, J. E., Samelson-Jones, B. J., George, L. A., Giermasz, A., Ducore, J. M., Teitel, J. M., McGuinn, C. E., High, K. A., Jong, Y. P. D., Chhabra, A., O’Brien, A., Smith, L. M., Winburn, I., Rupon, J. (2025). Fidanacogene Elaparvovec for Hemophilia B — A Multiyear Follow-up Study. New England Journal of Medicine. https://doi.org/10.1056/nejmoa2307159