Hanna, R., Frangoul, H., Pineiro, L., McKinney, C., Mapara, M., Dalal, J., Rangarajan, H. G., Atkins, H., Sharma, A., Chang, K., Jaskolka, M. C., Kim, K., Yu, Q., Mei, B., Afonja, O., Walters, M. C. (2026). CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease. New England Journal of Medicine. https://doi.org/10.1056/nejmoa2415550