Yongrong Lai, Rongrong Liu, Lijie Wang, Xu-Kai Ma, Yaliang Li, Gaohui Yang, Lingling Shi, Yi-Lin Guo, Zhenbin Wei, Xuemei Zhou, Wenchao Xu, Yaofeng Hou, Annarita Miccio, Bei Yang, Xiaodun Mou, Li Yang, Jia Chen. "Clinical application of base editing for treating β-thalassaemia." Nature (2026). https://doi.org/10.1038/s41586-026-10342-9