Yue Chai, Yao Zhu, Jiayi Zhu, Mingfeng Guan, Zhongyu Zheng, Yu Chen, Hayley Wing Sum Tsang, Tao Ye, Jacque Pak Kan Ip. "Base editing restores CDKL5 expression and rescues neuronal deficits in a patient-derived model of CDKL5 deficiency disorder." Scientific Reports, 2026. doi:10.1038/s41598-026-48097-y