Latour, R. P. D., Castro, C. D., Kelly, R., Kulasekararaj, A., Röth, A., Scheinberg, P., Ueda, Y., Applegate, D., Dahlke, M., Ferber, P., Schuhmann, I., Risitano, A. (2025). Apply-PNH: Analysis of complement pathway biomarkers provides evidence for pharmacodynamic response in PNH patients who receive oral iptacopan monotherapy versus continuing anti-C5 therapy. Blood. https://doi.org/10.1182/blood-2025-4979