Shamshul Huda, Mohan Kumar, Dikshika Bihani, Pratiksha Sarangi, Narendra Kumar, Dinesh Chandra, Giridhara Rao Jayandharan. "An engineered AAVrh10 vector containing an optimized factor IX transgene improves therapeutic response during hemophilia b gene therapy." Blood, 2025. doi:10.1182/blood-2025-6091