Liu, R., Wang, L., Xu, H., Fang, J., Liu, S., Yin, X., Liang, J., Li, X., Li, Y., Yang, G., Li, Y., Zhou, Y., Cheng, L., Lai, Y., Huang, J., Zhang, X. (2025). All 19 subjects with transfusion-dependent β-thalassemia achieved transfusion independence after treatment with RM-001 (autologous HBG1/2 promoter-modified CD34+ hematopoietic stem and progenitor cells). Blood. https://doi.org/10.1182/blood-2025-4308