Leticia Campoverde, Warren Fiskus, Jillian Mullin, Hiam Abdel-Salam, Danielle Hammond, Aishwarya Sahasrabudhe, Andrew Frelinger, Alan Cantor, Kapil Bhalla, Anupriya Agarwal, Courtney DiNardo. "A pilot study of low-dose sirolimus to increase hematopoietic function in patients with RUNX1 familial platelet disorder." Blood, 2025. doi:10.1182/blood-2025-1435